Challenges and Opportunities in Rare Pediatric Drug Development
From World Orphan Drug Congress 2021
Date: April 28, 2021
Barry Mangum, PharmD, FCP, Paidion
Betsy Reid, Paidion
Kristi Norris, PhD, Camargo
Over half of all rare diseases impact children. In this webinar, we’ll explore the pediatric drug development landscape and answer several key questions:
- Why is pediatric research important, and how is the life sciences industry evolving to address the research gap?
- What regulatory considerations are critical to success for development and approval of a new treatment for a rare pediatric disease?
- What can be done to improve pediatric clinical trials for children with rare diseases?